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- W4233054742 created "2022-05-12" @default.
- W4233054742 date "2019-06-14" @default.
- W4233054742 modified "2023-09-25" @default.
- W4233054742 title "Orphan designation: Modified messenger ribonucleic acid encoding human propionyl-coenzyme A carboxylase alpha and beta subunits encapsulated into lipid nanoparticle, Treatment of propionic acidaemia" @default.
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