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- Q58765137 name "Targeting Root Cause by Systemic scAAV9-h Gene Delivery: Functional Correction and Reversal of Severe MPS II in Mice" @default.
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- Q58765137 P1476 "Targeting Root Cause by Systemic scAAV9-h Gene Delivery: Functional Correction and Reversal of Severe MPS II in Mice" @default.
- Q58765137 P2093 "Aaron S Meadows" @default.
- Q58765137 P2093 "Douglas M McCarty" @default.
- Q58765137 P2093 "Haiyan Fu" @default.
- Q58765137 P2093 "Joseph Muenzer" @default.
- Q58765137 P2093 "Kim Zaraspe" @default.
- Q58765137 P2093 "Naoko Murakami" @default.
- Q58765137 P2093 "Ricardo J Pineda" @default.
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