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- Q59357429 name "Two breakthrough gene-targeted treatments for spinal muscular atrophy: challenges remain" @default.
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- Q59357429 P1476 "Two breakthrough gene-targeted treatments for spinal muscular atrophy: challenges remain" @default.
- Q59357429 P2093 "Charlotte J Sumner" @default.
- Q59357429 P2093 "Thomas O Crawford" @default.
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