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- Q64801755 description "clinical trial" @default.
- Q64801755 description "ensayu clínicu" @default.
- Q64801755 description "klinisch onderzoek" @default.
- Q64801755 description "клінічне випробування" @default.
- Q64801755 name "Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1" @default.
- Q64801755 type Item @default.
- Q64801755 label "Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1" @default.
- Q64801755 prefLabel "Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1" @default.
- Q64801755 P1050 Q64801755-69AD0FE8-3F63-4142-B7A4-112DAB0E487C @default.
- Q64801755 P1050 Q64801755-F41EC688-FEC6-4AF3-A0AE-18673DFB4A73 @default.
- Q64801755 P1132 Q64801755-66623736-2327-4CFC-8C4A-D595AC9C51A2 @default.
- Q64801755 P1476 Q64801755-19B0D540-25EC-4F49-87C4-C6E0D507CBFD @default.
- Q64801755 P17 Q64801755-04BA58DE-BDF6-42C1-ADA2-CC70C629E402 @default.
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- Q64801755 P17 Q64801755-124D39BA-72A4-46D8-AD14-E6F664B8EFDC @default.
- Q64801755 P17 Q64801755-480D6BA2-AA7D-4472-AA1F-069EE1F1A7E9 @default.
- Q64801755 P17 Q64801755-8EE7EBE5-EF49-4ED1-A031-158C8DABDDB8 @default.
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- Q64801755 P17 Q64801755-E43690A6-C74B-4352-815B-C86D8FFF20DB @default.
- Q64801755 P17 Q64801755-EFE34F77-4D85-4ADE-8FFC-A8195FB1B734 @default.
- Q64801755 P1813 Q64801755-4060596C-D8E8-4902-B814-0A64C63875AA @default.
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- Q64801755 P31 Q64801755-149DF3E5-D98E-4447-981E-ED47ED01E4CE @default.
- Q64801755 P4135 Q64801755-4BB92B86-4F8B-4BA7-A5F8-4FC523AA9001 @default.
- Q64801755 P580 Q64801755-25B63E1E-24F6-402C-A5E5-1FFA7F30D0A8 @default.
- Q64801755 P582 Q64801755-70C54E6C-5DFB-4DC2-AE09-35A930030BDF @default.
- Q64801755 P6099 Q64801755-9F08F351-3F19-4ED9-BF41-3F3EA64023FB @default.
- Q64801755 P6153 Q64801755-7E7FD6D0-3CA0-476E-946E-23AF4EAF8834 @default.
- Q64801755 P8363 Q64801755-43C53B18-5BA3-4CAA-94C3-ACBABF9BF09C @default.
- Q64801755 P1050 Q194520 @default.
- Q64801755 P1050 Q2844600 @default.
- Q64801755 P1132 "+30" @default.
- Q64801755 P1476 "European, Phase 3, Open-Label, Single-Arm, Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies Delivering AVXS-101 by Intravenous Infusion" @default.
- Q64801755 P17 Q142 @default.
- Q64801755 P17 Q145 @default.
- Q64801755 P17 Q183 @default.
- Q64801755 P17 Q29 @default.
- Q64801755 P17 Q31 @default.
- Q64801755 P17 Q34 @default.
- Q64801755 P17 Q38 @default.
- Q64801755 P17 Q55 @default.
- Q64801755 P1813 "STRIVE-EU" @default.
- Q64801755 P3098 "NCT03461289" @default.
- Q64801755 P31 Q30612 @default.
- Q64801755 P4135 "+6" @default.
- Q64801755 P580 "2018-08-29T00:00:00Z" @default.
- Q64801755 P582 "2020-11-01T00:00:00Z" @default.
- Q64801755 P6099 Q42824827 @default.
- Q64801755 P6153 Q46210 @default.
- Q64801755 P8363 Q78089383 @default.