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- Q93176751 description "article scientifique publié en 2020" @default.
- Q93176751 description "artículu científicu espublizáu n'abril de 2020" @default.
- Q93176751 description "scientific article published on 23 April 2020" @default.
- Q93176751 description "wetenschappelijk artikel" @default.
- Q93176751 description "наукова стаття, опублікована 23 квітня 2020" @default.
- Q93176751 name "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
- Q93176751 name "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
- Q93176751 type Item @default.
- Q93176751 label "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
- Q93176751 label "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
- Q93176751 prefLabel "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
- Q93176751 prefLabel "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
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- Q93176751 P1476 Q93176751-18518A07-29AF-4CAB-9AFB-FACCEC91ABD9 @default.
- Q93176751 P2093 Q93176751-03CDF145-D708-48BD-9309-0D29CE0EA5F3 @default.
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- Q93176751 P31 Q93176751-693968F8-8A45-4221-ABAA-C7658FE2B065 @default.
- Q93176751 P356 Q93176751-8BAB3A65-7B6E-412E-BCE6-E7190B8C540F @default.
- Q93176751 P50 Q93176751-D02F1602-84A5-446F-BDE8-8EBB09C2A672 @default.
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- Q93176751 P698 Q93176751-B4A97BAF-E41A-4384-9132-6A1DAC78F25F @default.
- Q93176751 P921 Q93176751-C5D28374-6E10-4B43-8641-34CFC975B83A @default.
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- Q93176751 P932 Q93176751-DA59ADFA-15CD-4B45-9E96-1DA66F2D0DE0 @default.
- Q93176751 P356 JIMD.12245 @default.
- Q93176751 P698 32324281 @default.
- Q93176751 P1433 Q6295359 @default.
- Q93176751 P1476 "Long-term survival outcomes of patients with Niemann-Pick disease type C receiving miglustat treatment: a large retrospective observational study" @default.
- Q93176751 P2093 "B Héron" @default.
- Q93176751 P2093 "B Schwierin" @default.
- Q93176751 P2093 "D Rosenberg" @default.
- Q93176751 P2093 "F J Meaney" @default.
- Q93176751 P2093 "H Jahnova" @default.
- Q93176751 P2093 "J Imrie" @default.
- Q93176751 P2093 "M T Vanier" @default.
- Q93176751 P2093 "O Morand" @default.
- Q93176751 P2093 "P Moneuse" @default.
- Q93176751 P2093 "W S Garver" @default.
- Q93176751 P2093 "Y Nadjar" @default.
- Q93176751 P31 Q13442814 @default.
- Q93176751 P356 "10.1002/JIMD.12245" @default.
- Q93176751 P50 Q39031058 @default.
- Q93176751 P50 Q47118822 @default.
- Q93176751 P577 "2020-04-23T00:00:00Z" @default.
- Q93176751 P698 "32324281" @default.
- Q93176751 P921 Q1419931 @default.
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