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- W1973269732 endingPage "1268" @default.
- W1973269732 startingPage "1252" @default.
- W1973269732 abstract "Gene therapy is a potentially potent new method of treating a number of neurologic disorders previously considered refractory to current conventional therapeutic treatments. Numerous advances have been made in the construction of expression vectors, cellular and viral transgene carriers, and the characterization of target cells for neuronal gene therapy. Two primary approaches to nervous system gene transfer have emerged as a result of these advances. The in vivo approach concentrates on direct transfer of genetic material to cells in vivo using viral and chemical agents. The ex vivo approach relies on genetic transfer to cultured cells that are subsequently implanted into a host organism. Both of these methods have been used in preliminary experiments designed to test the efficacy of gene transfer strategies in the amelioration of nervous system dysfunction." @default.
- W1973269732 created "2016-06-24" @default.
- W1973269732 creator A5025914931 @default.
- W1973269732 creator A5072968010 @default.
- W1973269732 date "1993-11-01" @default.
- W1973269732 modified "2023-09-23" @default.
- W1973269732 title "Gene Therapy for Neurologic Disease" @default.
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