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- W1982360586 abstract "Inherited retinal and choroidal degenerations account for a significant portion of blindness in children and young adults. This article reviews the current status and future prospects for the treatment of these disorders. Current treatment strategies include nutritional intervention for gyrate atrophy of the choroid and retina with hyperornithinemia, abetalipoproteinemia, and Refsum's disease, as well as vitamin A supplementation for retinitis pigmentosa. Future therapeutic prospects include gene therapy for both recessive and dominant disease, secondary gene-based therapies, such as pharmaceutic gene product replacement and treatment with survival factors, anti-apoptotic agents, and calcium blockers, and, finally, stem cell therapy." @default.
- W1982360586 created "2016-06-24" @default.
- W1982360586 creator A5036422156 @default.
- W1982360586 creator A5059961090 @default.
- W1982360586 creator A5089443897 @default.
- W1982360586 date "2003-12-01" @default.
- W1982360586 modified "2023-10-07" @default.
- W1982360586 title "Treatment of retinal and choroidal degenerations and dystrophies: current status and prospects for gene-based therapy" @default.
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