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- W2000708840 abstract "Lentiviral vectors are widely used in experimental gene transfer and are a promising tool for clinical applications, particularly for the treatment of neurodegenerative diseases. However, one of the most important limits to the application of this technology to humans is the risk of insertional mutagenesis through the integration of the viral genome into the host cell chromatin. This risk remains poorly evaluated and uncontrolled. In order to eliminate this risk, we have developed a lentiviral vector derived from the human immunodeficiency virus type 1 lacking integration property. After cell transduction, the vector genome persists in an extrachromosomic circular form in the nucleus and allows an effective and stable transgene expression in vitro and in vivo." @default.
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- W2000708840 date "2005-05-01" @default.
- W2000708840 modified "2023-09-23" @default.
- W2000708840 title "92. Efficient Trangene Expression in Central Nervous System through a Non-Integrative Lentiviral Vector" @default.
- W2000708840 doi "https://doi.org/10.1016/j.ymthe.2005.06.098" @default.
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