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- W2003754695 abstract "Despite the passage of more than 15 years since the identification of the first polyglutamine disease-causing mutation, many unanswered questions about the etiologies of these disorders remain. This review discusses the major areas of suspected dysfunction, with an emphasis on recent literature. In addition, it attempts to associate the implicated disease mechanisms with the therapeutic targets likely to be explored in the near- and mid-range future." @default.
- W2003754695 created "2016-06-24" @default.
- W2003754695 creator A5071837576 @default.
- W2003754695 date "2007-06-01" @default.
- W2003754695 modified "2023-10-14" @default.
- W2003754695 title "Huntington's and other polyglutamine diseases: many effects of single gene mutations" @default.
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- W2003754695 doi "https://doi.org/10.1016/j.ddmec.2007.10.002" @default.
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