Matches in SemOpenAlex for { <https://semopenalex.org/work/W2012386055> ?p ?o ?g. }
- W2012386055 endingPage "310" @default.
- W2012386055 startingPage "299" @default.
- W2012386055 abstract "The development of therapeutic strategies that overcome the unique problems posed by Duchenne muscular dystrophy (DMD) has lead to the development of many contemporary approaches to human disease in general. Various treatment approaches have been explored--such as pharmacological therapies and cell-based, cytokine, and genetic therapies--that are all targeted to specific features of dystrophic DMD muscle pathology. In genetic therapies, the large size of the dystrophin gene has necessitated the development and use of novel functional minidystrophin and microdystrophin genes, muscle-specific promoter systems, and gutted adenoviral systems. In addition to these well defined viral strategies, plasmid vectors and the upregulation of utrophin (a dystrophin homologue) have potential. Various novel genetic approaches--such as antisense-mediated exon skipping, gene correction, and new cytokine approaches--are also being developed. Together these exciting developments bring an effective treatment for DMD closer than ever before." @default.
- W2012386055 created "2016-06-24" @default.
- W2012386055 creator A5011401177 @default.
- W2012386055 creator A5015407623 @default.
- W2012386055 creator A5051775643 @default.
- W2012386055 date "2003-05-01" @default.
- W2012386055 modified "2023-10-11" @default.
- W2012386055 title "Novel therapies for Duchenne muscular dystrophy" @default.
- W2012386055 cites W1515542606 @default.
- W2012386055 cites W1519383882 @default.
- W2012386055 cites W1525067447 @default.
- W2012386055 cites W1586130277 @default.
- W2012386055 cites W192719192 @default.
- W2012386055 cites W1963528166 @default.
- W2012386055 cites W1964733523 @default.
- W2012386055 cites W1966613997 @default.
- W2012386055 cites W1967391351 @default.
- W2012386055 cites W1972049148 @default.
- W2012386055 cites W1972575220 @default.
- W2012386055 cites W1973487567 @default.
- W2012386055 cites W1974140457 @default.
- W2012386055 cites W1978507399 @default.
- W2012386055 cites W1981141119 @default.
- W2012386055 cites W1983555241 @default.
- W2012386055 cites W1983599089 @default.
- W2012386055 cites W1986088843 @default.
- W2012386055 cites W1986390617 @default.
- W2012386055 cites W1988269377 @default.
- W2012386055 cites W1988749764 @default.
- W2012386055 cites W1988900658 @default.
- W2012386055 cites W1988936141 @default.
- W2012386055 cites W1990748900 @default.
- W2012386055 cites W1991248271 @default.
- W2012386055 cites W1992677182 @default.
- W2012386055 cites W1993834457 @default.
- W2012386055 cites W2004908650 @default.
- W2012386055 cites W2006683789 @default.
- W2012386055 cites W2011767474 @default.
- W2012386055 cites W2012545917 @default.
- W2012386055 cites W2013028019 @default.
- W2012386055 cites W2013074698 @default.
- W2012386055 cites W2014543704 @default.
- W2012386055 cites W2015631186 @default.
- W2012386055 cites W2016253997 @default.
- W2012386055 cites W2018600945 @default.
- W2012386055 cites W2018744718 @default.
- W2012386055 cites W2018823858 @default.
- W2012386055 cites W2019563312 @default.
- W2012386055 cites W2023254910 @default.
- W2012386055 cites W2023972061 @default.
- W2012386055 cites W2025500946 @default.
- W2012386055 cites W2028930741 @default.
- W2012386055 cites W2029158145 @default.
- W2012386055 cites W2033271861 @default.
- W2012386055 cites W2035051422 @default.
- W2012386055 cites W2038491737 @default.
- W2012386055 cites W2044648356 @default.
- W2012386055 cites W2045584725 @default.
- W2012386055 cites W2048864017 @default.
- W2012386055 cites W2049222776 @default.
- W2012386055 cites W2051189314 @default.
- W2012386055 cites W2051442157 @default.
- W2012386055 cites W2053191459 @default.
- W2012386055 cites W2058807250 @default.
- W2012386055 cites W2060628728 @default.
- W2012386055 cites W2061555550 @default.
- W2012386055 cites W2062867597 @default.
- W2012386055 cites W2062892149 @default.
- W2012386055 cites W2064432309 @default.
- W2012386055 cites W2064788529 @default.
- W2012386055 cites W2065009763 @default.
- W2012386055 cites W2065704959 @default.
- W2012386055 cites W2066180106 @default.
- W2012386055 cites W2067189573 @default.
- W2012386055 cites W2068350301 @default.
- W2012386055 cites W2068549450 @default.
- W2012386055 cites W2070936696 @default.
- W2012386055 cites W2072784433 @default.
- W2012386055 cites W2072847969 @default.
- W2012386055 cites W2073371551 @default.
- W2012386055 cites W2073377967 @default.
- W2012386055 cites W2075271276 @default.
- W2012386055 cites W2076440327 @default.
- W2012386055 cites W2076462595 @default.
- W2012386055 cites W2077224588 @default.
- W2012386055 cites W2079870275 @default.
- W2012386055 cites W2080234756 @default.
- W2012386055 cites W2081158661 @default.
- W2012386055 cites W2083700023 @default.
- W2012386055 cites W2084936584 @default.
- W2012386055 cites W2087300469 @default.
- W2012386055 cites W2089807223 @default.
- W2012386055 cites W2091163726 @default.
- W2012386055 cites W2093052874 @default.
- W2012386055 cites W2093377166 @default.
- W2012386055 cites W2100682779 @default.
- W2012386055 cites W2101579071 @default.
- W2012386055 cites W2101685875 @default.