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- W2017782024 endingPage "1271" @default.
- W2017782024 startingPage "1257" @default.
- W2017782024 abstract "Introduction: Fetal gene therapy (FGT) can potentially be applied to perinatally lethal monogenic diseases for rescuing clinically severe phenotypes, increasing the probability of intact neurological and other key functions at birth, or inducing immune tolerance to a transgenic protein to facilitate readministration of the vector/protein postnatally. As the field is still at an experimental stage, there are several important considerations regarding the practicality and the ethics of FGT. Areas covered: Here, through a review of FGT studies, the authors discuss the role and applications of FGT, the progress made with animal models that simulate human development, possible adverse effects in the recipient fetus and the mother and factors that affect clinical translation. Expert opinion: Although there are valid safety and ethical concerns, the authors argue that there may soon be enough convincing evidence from non-human primate models to take the next step towards clinical trials in the near future." @default.
- W2017782024 created "2016-06-24" @default.
- W2017782024 creator A5026999314 @default.
- W2017782024 creator A5030659181 @default.
- W2017782024 creator A5055882688 @default.
- W2017782024 creator A5075249092 @default.
- W2017782024 creator A5085326777 @default.
- W2017782024 date "2011-05-31" @default.
- W2017782024 modified "2023-09-30" @default.
- W2017782024 title "Fetal gene therapy: recent advances and current challenges" @default.
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