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- W2020106352 endingPage "507" @default.
- W2020106352 startingPage "499" @default.
- W2020106352 abstract "Myotonic dystrophy (DM) is a dominantly inherited, multisystemic disease caused by expanded CTG (type 1, DM1) or CCTG (type 2, DM2) repeats in untranslated regions of the mutated genes. Pathogenesis results from expression of RNAs from the mutated alleles that are toxic because of the expanded CUG or CCUG repeats. Increased understanding of the repeat-containing RNA (C/CUG(exp) RNA)-induced toxicity has led to the development of multiple strategies targeting the toxic RNA. Among these approaches, antisense oligonucleotides (ASOs) have demonstrated high potency in reversing the RNA toxicity in both cultured DM1 cells and DM1 animal models, thus offering great promise for the potential treatment of DM1. ASO targeting approaches will also provide avenues for the treatment of other repeat RNA-mediated diseases." @default.
- W2020106352 created "2016-06-24" @default.
- W2020106352 creator A5013019099 @default.
- W2020106352 creator A5089541883 @default.
- W2020106352 date "2013-05-01" @default.
- W2020106352 modified "2023-09-23" @default.
- W2020106352 title "Antisense Oligonucleotides: Rising Stars in Eliminating RNA Toxicity in Myotonic Dystrophy" @default.
- W2020106352 cites W146584691 @default.
- W2020106352 cites W1542302893 @default.
- W2020106352 cites W1555409852 @default.
- W2020106352 cites W1964008557 @default.
- W2020106352 cites W1967470178 @default.
- W2020106352 cites W1968949098 @default.
- W2020106352 cites W1969325395 @default.
- W2020106352 cites W1972453061 @default.
- W2020106352 cites W1972704271 @default.
- W2020106352 cites W1975664052 @default.
- W2020106352 cites W1977510643 @default.
- W2020106352 cites W1984223300 @default.
- W2020106352 cites W1990059209 @default.
- W2020106352 cites W1992481904 @default.
- W2020106352 cites W1994495307 @default.
- W2020106352 cites W1994674028 @default.
- W2020106352 cites W1995397443 @default.
- W2020106352 cites W1999711632 @default.
- W2020106352 cites W2000725203 @default.
- W2020106352 cites W2001607290 @default.
- W2020106352 cites W2001698040 @default.
- W2020106352 cites W2003576322 @default.
- W2020106352 cites W2004824383 @default.
- W2020106352 cites W2004901342 @default.
- W2020106352 cites W2006167464 @default.
- W2020106352 cites W2007145717 @default.
- W2020106352 cites W2009372610 @default.
- W2020106352 cites W2009800290 @default.
- W2020106352 cites W2010757394 @default.
- W2020106352 cites W2011049276 @default.
- W2020106352 cites W2012195419 @default.
- W2020106352 cites W2013317908 @default.
- W2020106352 cites W2013963839 @default.
- W2020106352 cites W2020334159 @default.
- W2020106352 cites W2022996403 @default.
- W2020106352 cites W2025816722 @default.
- W2020106352 cites W2025855695 @default.
- W2020106352 cites W2030515818 @default.
- W2020106352 cites W2034040174 @default.
- W2020106352 cites W2036075451 @default.
- W2020106352 cites W2038306358 @default.
- W2020106352 cites W2038354607 @default.
- W2020106352 cites W2039364812 @default.
- W2020106352 cites W2041385249 @default.
- W2020106352 cites W2045953719 @default.
- W2020106352 cites W2048359227 @default.
- W2020106352 cites W2050193524 @default.
- W2020106352 cites W2057338624 @default.
- W2020106352 cites W2063685191 @default.
- W2020106352 cites W2063936397 @default.
- W2020106352 cites W2066174868 @default.
- W2020106352 cites W2071746751 @default.
- W2020106352 cites W2073289591 @default.
- W2020106352 cites W2076324093 @default.
- W2020106352 cites W2081280332 @default.
- W2020106352 cites W2081748748 @default.
- W2020106352 cites W2082965230 @default.
- W2020106352 cites W2084091637 @default.
- W2020106352 cites W2085124069 @default.
- W2020106352 cites W2088201490 @default.
- W2020106352 cites W2092574488 @default.
- W2020106352 cites W2092831145 @default.
- W2020106352 cites W2099455170 @default.
- W2020106352 cites W2103059478 @default.
- W2020106352 cites W2104345366 @default.
- W2020106352 cites W2110459103 @default.
- W2020106352 cites W2110640321 @default.
- W2020106352 cites W2112159040 @default.
- W2020106352 cites W2113525941 @default.
- W2020106352 cites W2113918626 @default.
- W2020106352 cites W2121453437 @default.
- W2020106352 cites W2123193865 @default.
- W2020106352 cites W2123356145 @default.
- W2020106352 cites W2123557978 @default.
- W2020106352 cites W2127118078 @default.
- W2020106352 cites W2128578017 @default.
- W2020106352 cites W2129286776 @default.
- W2020106352 cites W2129611261 @default.
- W2020106352 cites W2129718981 @default.
- W2020106352 cites W2130803788 @default.
- W2020106352 cites W2130886644 @default.
- W2020106352 cites W2131447660 @default.
- W2020106352 cites W2132852866 @default.
- W2020106352 cites W2135118216 @default.
- W2020106352 cites W2136930242 @default.
- W2020106352 cites W2139919925 @default.
- W2020106352 cites W2140074138 @default.
- W2020106352 cites W2141124826 @default.
- W2020106352 cites W2146234141 @default.
- W2020106352 cites W2150523249 @default.
- W2020106352 cites W2153427615 @default.