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- W2021007455 abstract "Hematopoietic stem cell gene therapy is potentially curative for a number of inherited and acquired disorders. However, poor gene transfer and expression in repopulating hematopoietic stem cells attenuate this potential. Here we review potential means of conferring a selective advantage to hematopoietic stem cells and their progeny, and discuss the issues that surround the use of selective advantages in vivo." @default.
- W2021007455 created "2016-06-24" @default.
- W2021007455 creator A5060799881 @default.
- W2021007455 creator A5067898898 @default.
- W2021007455 date "2004-02-01" @default.
- W2021007455 modified "2023-10-18" @default.
- W2021007455 title "Protection and selection for gene therapy in the hematopoietic system" @default.
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