Matches in SemOpenAlex for { <https://semopenalex.org/work/W2023771021> ?p ?o ?g. }
- W2023771021 abstract "Primary systemic vasculitides of the young are relatively rare diseases, but are associated with significant morbidity and mortality, particularly if there is diagnostic delay. We provide an overview of paediatric vasculitides with emphasis on key differences in vasculitis presentation and management between children and adults. Significant advances in the field of paediatric vasculitis research include the development of classification criteria and disease outcome tools for paediatric disease; inclusion of paediatric patients in international multicentre randomized controlled trials of therapies in vasculitis; and development of rare disease trial designs for therapeutic trials of paediatric vasculitis. The continuation of unmet needs as well as the exploration of potential therapeutic avenues and considerations in the design of future trials are also discussed." @default.
- W2023771021 created "2016-06-24" @default.
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- W2023771021 date "2014-12-30" @default.
- W2023771021 modified "2023-10-17" @default.
- W2023771021 title "Vasculitis in children" @default.
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- W2023771021 doi "https://doi.org/10.1093/ndt/gfu393" @default.
- W2023771021 hasPubMedId "https://pubmed.ncbi.nlm.nih.gov/25550447" @default.
- W2023771021 hasPublicationYear "2014" @default.
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