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- W2068691970 endingPage "1267" @default.
- W2068691970 startingPage "1259" @default.
- W2068691970 abstract "Gene transfer targeting cells of the blood and immune system was one of the first areas of investigation in the field of gene therapy. Despite the encouraging results achieved in early studies using murine bone marrow, the task of gene transfer into human hematopoietic stem cells proved to be far more difficult. As a result, progress has been disappointingly slow and initial clinical trials generally failed to achieve significant levels of gene marking. The continued application of new advances in vectorology and hematopoietic stem cell biology has now led to improvements in preclinical models that are being translated into clinical trials. The progress and remaining problems are discussed in this review article." @default.
- W2068691970 created "2016-06-24" @default.
- W2068691970 creator A5050109992 @default.
- W2068691970 creator A5054557581 @default.
- W2068691970 date "2000-06-10" @default.
- W2068691970 modified "2023-10-16" @default.
- W2068691970 title "Gene Therapy Using Hematopoietic Stem Cells: Sisyphus Approaches the Crest" @default.
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- W2068691970 doi "https://doi.org/10.1089/10430340050032366" @default.
- W2068691970 hasPubMedId "https://pubmed.ncbi.nlm.nih.gov/10890736" @default.
- W2068691970 hasPublicationYear "2000" @default.