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- W2074977276 endingPage "86" @default.
- W2074977276 startingPage "69" @default.
- W2074977276 abstract "Alternative splicing is an important regulator of the transcriptome. However, mutations may cause alteration of splicing patterns, which in turn leads to disease. During the past 10 years, exon skipping has been looked upon as a powerful tool for correction of missplicing in disease and progress has been made towards clinical trials. In this review, we discuss the use of antisense oligonucleotides to correct splicing defects through exon skipping, with a special focus on diseases affecting the nervous system, and the latest stage achieved in its progress." @default.
- W2074977276 created "2016-06-24" @default.
- W2074977276 creator A5020562782 @default.
- W2074977276 creator A5056772593 @default.
- W2074977276 creator A5082100902 @default.
- W2074977276 date "2014-02-01" @default.
- W2074977276 modified "2023-10-16" @default.
- W2074977276 title "Exon-Skipping Antisense Oligonucleotides to Correct Missplicing in Neurogenetic Diseases" @default.
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