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- W2078340108 endingPage "106" @default.
- W2078340108 startingPage "88" @default.
- W2078340108 abstract "The cloning of the dystrophin gene has led to major advances in the understanding of the molecular genetic basis of Duchenne, Becker, and other muscular dystrophies associated with mutations in genes encoding members of the dystrophin-associated glycoprotein complex. The recent introduction of pharmaceutical agents such as prednisone has shown great promise in delaying the progression of Duchenne muscular dystrophy but there remains a need to develop more long-term therapeutic interventions. Knowledge of the nature of the dystrophin gene and the glycoprotein complex has led many researchers to think that somatic gene replacement represents the most promising approach to treatment. The potential use of this strategy has been shown in the mdx mouse model of Duchenne muscular dystrophy, where germ line gene transfer of either a full-length or a smaller Becker-type dystrophin minigene prevents necrosis and restores normal muscle function." @default.
- W2078340108 created "2016-06-24" @default.
- W2078340108 creator A5025336192 @default.
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- W2078340108 creator A5069821486 @default.
- W2078340108 creator A5069866048 @default.
- W2078340108 date "2002-08-01" @default.
- W2078340108 modified "2023-10-18" @default.
- W2078340108 title "Duchenne Muscular Dystrophy: Current Knowledge, Treatment, and Future Prospects" @default.
- W2078340108 cites W10680619 @default.
- W2078340108 cites W1482504262 @default.
- W2078340108 cites W1497143641 @default.
- W2078340108 cites W1515941828 @default.
- W2078340108 cites W1530583566 @default.
- W2078340108 cites W1574658543 @default.
- W2078340108 cites W1632349675 @default.
- W2078340108 cites W174097160 @default.
- W2078340108 cites W1748445510 @default.
- W2078340108 cites W1957992664 @default.
- W2078340108 cites W1965858834 @default.
- W2078340108 cites W1966791163 @default.
- W2078340108 cites W1967261851 @default.
- W2078340108 cites W1968325292 @default.
- W2078340108 cites W1968666078 @default.
- W2078340108 cites W1969113601 @default.
- W2078340108 cites W1969570221 @default.
- W2078340108 cites W1970561503 @default.
- W2078340108 cites W1970657278 @default.
- W2078340108 cites W1973487567 @default.
- W2078340108 cites W1973546377 @default.
- W2078340108 cites W1973774525 @default.
- W2078340108 cites W1974891606 @default.
- W2078340108 cites W1975884987 @default.
- W2078340108 cites W1976323848 @default.
- W2078340108 cites W1976753246 @default.
- W2078340108 cites W1977362203 @default.
- W2078340108 cites W1977394169 @default.
- W2078340108 cites W1979599456 @default.
- W2078340108 cites W1981850472 @default.
- W2078340108 cites W1983673827 @default.
- W2078340108 cites W1988900658 @default.
- W2078340108 cites W1989633007 @default.
- W2078340108 cites W1990561446 @default.
- W2078340108 cites W1990748900 @default.
- W2078340108 cites W1990907625 @default.
- W2078340108 cites W1991248271 @default.
- W2078340108 cites W1991455835 @default.
- W2078340108 cites W1991607969 @default.
- W2078340108 cites W1993026635 @default.
- W2078340108 cites W1994805392 @default.
- W2078340108 cites W1995635449 @default.
- W2078340108 cites W1998484472 @default.
- W2078340108 cites W1998536172 @default.
- W2078340108 cites W1998663807 @default.
- W2078340108 cites W2001927982 @default.
- W2078340108 cites W2003730995 @default.
- W2078340108 cites W2005402291 @default.
- W2078340108 cites W2007942167 @default.
- W2078340108 cites W2008115339 @default.
- W2078340108 cites W2008443058 @default.
- W2078340108 cites W2011767474 @default.
- W2078340108 cites W2012265849 @default.
- W2078340108 cites W2012545917 @default.
- W2078340108 cites W2014010760 @default.
- W2078340108 cites W2014495927 @default.
- W2078340108 cites W2015219383 @default.
- W2078340108 cites W2018477101 @default.
- W2078340108 cites W2020217527 @default.
- W2078340108 cites W2020623610 @default.
- W2078340108 cites W2021135182 @default.
- W2078340108 cites W2023315897 @default.
- W2078340108 cites W2024397909 @default.
- W2078340108 cites W2025791374 @default.
- W2078340108 cites W2026728314 @default.
- W2078340108 cites W2027345413 @default.
- W2078340108 cites W2028134688 @default.
- W2078340108 cites W2030810535 @default.
- W2078340108 cites W2034654629 @default.
- W2078340108 cites W2036426068 @default.
- W2078340108 cites W2038642657 @default.
- W2078340108 cites W2038783161 @default.
- W2078340108 cites W2038978204 @default.
- W2078340108 cites W2040507881 @default.
- W2078340108 cites W2041208030 @default.
- W2078340108 cites W2043317882 @default.
- W2078340108 cites W2046966094 @default.
- W2078340108 cites W2047330128 @default.
- W2078340108 cites W2048347092 @default.
- W2078340108 cites W2049222776 @default.
- W2078340108 cites W2050087745 @default.
- W2078340108 cites W2051027468 @default.
- W2078340108 cites W2051033051 @default.
- W2078340108 cites W2051189314 @default.
- W2078340108 cites W2053920975 @default.
- W2078340108 cites W2055121141 @default.
- W2078340108 cites W2056330275 @default.
- W2078340108 cites W2057313033 @default.