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- W2078348892 endingPage "599" @default.
- W2078348892 startingPage "589" @default.
- W2078348892 abstract "Hematopoietic stem cells constitute a rare population of precursor cells with remarkable properties for being used as targets in gene therapy protocols. The last years have been particularly productive both in the fields of gene therapy and stem cell biology. Results from ongoing clinical trials have shown the first unquestionable clinical benefits of immunodeficient patients transplanted with genetically modified autologous stem cells. On the other hand, severe side effects in a few patients treated with gene therapy have also been reported, indicating the usefulness of further improving the vectors currently used in gene therapy clinical trials. In the field of stem cell biology, evidence showing the plastic potential of adult hematopoietic stem cells and data indicating the multipotency of adult mesenchymal precursor cells have been presented. Also, the generation of embryonic stem cells by means of nuclear transfer techniques has appeared as a new methodology with direct implications in gene therapy." @default.
- W2078348892 created "2016-06-24" @default.
- W2078348892 creator A5003429159 @default.
- W2078348892 creator A5043526837 @default.
- W2078348892 creator A5058916695 @default.
- W2078348892 creator A5069870899 @default.
- W2078348892 creator A5090896983 @default.
- W2078348892 date "2003-11-01" @default.
- W2078348892 modified "2023-09-24" @default.
- W2078348892 title "Genetic modification of hematopoietic stem cells: recent advances in the gene therapy of inherited diseases" @default.
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