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- W2109157099 abstract "Fatigue is a common and often disabling symptom among both mildly and severely affected adult patients with Pompe disease. Our objective was to determine whether enzyme replacement therapy (ERT) reduces fatigue in adult patients with Pompe disease." @default.
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- W2109157099 date "2013-05-01" @default.
- W2109157099 modified "2023-09-30" @default.
- W2109157099 title "Enzyme replacement therapy and fatigue in adults with Pompe disease" @default.
- W2109157099 doi "https://doi.org/10.1186/1471-2474-14-s2-p16" @default.
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