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- W2164295449 abstract "Phenylbutyrate enhances pyruvate dehydrogenase enzyme complex (PDHC) activity through inhibition of PDHC kinase, rescues the severe phenotype of a zebrafish model of PDHC deficiency, and prevents systemic lactic acidosis." @default.
- W2164295449 created "2016-06-24" @default.
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- W2164295449 date "2013-03-06" @default.
- W2164295449 modified "2023-10-01" @default.
- W2164295449 title "Phenylbutyrate Therapy for Pyruvate Dehydrogenase Complex Deficiency and Lactic Acidosis" @default.
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- W2164295449 doi "https://doi.org/10.1126/scitranslmed.3004986" @default.
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