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- W2187507029 abstract "Inherited diseases of retinal degeneration such as retinitis pigmentosa (RP) are characterized by progressive loss of photoreceptor cells in the retina. These hereditary disorders are potentially treatable with gene therapy; however, in the clinic, gene replacement through viral vector delivery of" @default.
- W2187507029 created "2016-06-24" @default.
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- W2187507029 date "2015-09-30" @default.
- W2187507029 modified "2023-09-26" @default.
- W2187507029 title "Boosting the success of retinal gene therapy" @default.
- W2187507029 doi "https://doi.org/10.1126/scitranslmed.aad3065" @default.
- W2187507029 hasPublicationYear "2015" @default.
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