Matches in SemOpenAlex for { <https://semopenalex.org/work/W2410443574> ?p ?o ?g. }
Showing items 1 to 75 of
75
with 100 items per page.
- W2410443574 endingPage "28" @default.
- W2410443574 startingPage "26" @default.
- W2410443574 abstract "Abstract AAV-mediated gene therapy has the potential to be paradigm shifting as a treatment for haemophilia. A single administration of AAV vector can result in safe and consistent long-term expression of transgene (>5 years), reduction in spontaneous bleeding episodes, reduction in clotting factor usage and an improvement in quality of life. There is huge commercial interest in this approach, with the expectation that an AAV gene therapy product for haemophilia B will be licensed by 2020." @default.
- W2410443574 created "2016-06-24" @default.
- W2410443574 creator A5032635874 @default.
- W2410443574 date "2015-07-01" @default.
- W2410443574 modified "2023-09-24" @default.
- W2410443574 title "Gene therapy for haemophilia: a very modern success story" @default.
- W2410443574 cites W2122304523 @default.
- W2410443574 cites W2400284658 @default.
- W2410443574 doi "https://doi.org/10.17225/jhp00058" @default.
- W2410443574 hasPublicationYear "2015" @default.
- W2410443574 type Work @default.
- W2410443574 sameAs 2410443574 @default.
- W2410443574 citedByCount "0" @default.
- W2410443574 crossrefType "journal-article" @default.
- W2410443574 hasAuthorship W2410443574A5032635874 @default.
- W2410443574 hasBestOaLocation W24104435741 @default.
- W2410443574 hasConcept C104317684 @default.
- W2410443574 hasConcept C104863432 @default.
- W2410443574 hasConcept C111599444 @default.
- W2410443574 hasConcept C126322002 @default.
- W2410443574 hasConcept C141071460 @default.
- W2410443574 hasConcept C159110408 @default.
- W2410443574 hasConcept C177713679 @default.
- W2410443574 hasConcept C2777081929 @default.
- W2410443574 hasConcept C2777232031 @default.
- W2410443574 hasConcept C2778385053 @default.
- W2410443574 hasConcept C2779951463 @default.
- W2410443574 hasConcept C2781221834 @default.
- W2410443574 hasConcept C2992139802 @default.
- W2410443574 hasConcept C3018928802 @default.
- W2410443574 hasConcept C512399662 @default.
- W2410443574 hasConcept C54355233 @default.
- W2410443574 hasConcept C60644358 @default.
- W2410443574 hasConcept C71924100 @default.
- W2410443574 hasConcept C86803240 @default.
- W2410443574 hasConceptScore W2410443574C104317684 @default.
- W2410443574 hasConceptScore W2410443574C104863432 @default.
- W2410443574 hasConceptScore W2410443574C111599444 @default.
- W2410443574 hasConceptScore W2410443574C126322002 @default.
- W2410443574 hasConceptScore W2410443574C141071460 @default.
- W2410443574 hasConceptScore W2410443574C159110408 @default.
- W2410443574 hasConceptScore W2410443574C177713679 @default.
- W2410443574 hasConceptScore W2410443574C2777081929 @default.
- W2410443574 hasConceptScore W2410443574C2777232031 @default.
- W2410443574 hasConceptScore W2410443574C2778385053 @default.
- W2410443574 hasConceptScore W2410443574C2779951463 @default.
- W2410443574 hasConceptScore W2410443574C2781221834 @default.
- W2410443574 hasConceptScore W2410443574C2992139802 @default.
- W2410443574 hasConceptScore W2410443574C3018928802 @default.
- W2410443574 hasConceptScore W2410443574C512399662 @default.
- W2410443574 hasConceptScore W2410443574C54355233 @default.
- W2410443574 hasConceptScore W2410443574C60644358 @default.
- W2410443574 hasConceptScore W2410443574C71924100 @default.
- W2410443574 hasConceptScore W2410443574C86803240 @default.
- W2410443574 hasIssue "2" @default.
- W2410443574 hasLocation W24104435741 @default.
- W2410443574 hasOpenAccess W2410443574 @default.
- W2410443574 hasPrimaryLocation W24104435741 @default.
- W2410443574 hasRelatedWork W173472931 @default.
- W2410443574 hasRelatedWork W1971613351 @default.
- W2410443574 hasRelatedWork W2049592320 @default.
- W2410443574 hasRelatedWork W2056645358 @default.
- W2410443574 hasRelatedWork W2160761181 @default.
- W2410443574 hasRelatedWork W2340607652 @default.
- W2410443574 hasRelatedWork W240105960 @default.
- W2410443574 hasRelatedWork W2410443574 @default.
- W2410443574 hasRelatedWork W2419438366 @default.
- W2410443574 hasRelatedWork W2924734268 @default.
- W2410443574 hasVolume "2" @default.
- W2410443574 isParatext "false" @default.
- W2410443574 isRetracted "false" @default.
- W2410443574 magId "2410443574" @default.
- W2410443574 workType "article" @default.