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- W2477852672 endingPage "130" @default.
- W2477852672 startingPage "103" @default.
- W2477852672 abstract "The recent development of recombinant viral vectors that are capable of transducing postmitotic cells may provide a powerful new tool for studying brain function, as well as ameliorative strategies in models of neurological disease. Some of these vectors have recently demonstrated direct expression of biologically relevant levels of protein expression (, ; ; ) for varying periods of time of up to 1 yr after direct intracerebral injection (, ; ; ). Moreover, vectors injected into the nervous system have been shown, not only to be capable of expressing de novo transgenes, but also to be able to regionally suppress gene expression by delivery of antisense oligonucleotides (), by expression of a dominant-negative protein, by local knock-out of genes in transgenic animals carrying a transgene surrounded by lox-P sites (), or by the production of molecules capable of inhibiting specific mRNAs, called ribozymes (). Thus, the use of viral vectors has great potential, not only for the study of gene therapy (GT), but also for the study of the molecular basis of certain brain functions." @default.
- W2477852672 created "2016-08-23" @default.
- W2477852672 creator A5016875954 @default.
- W2477852672 creator A5040767963 @default.
- W2477852672 creator A5064494707 @default.
- W2477852672 creator A5069700353 @default.
- W2477852672 creator A5078278744 @default.
- W2477852672 date "2000-01-01" @default.
- W2477852672 modified "2023-09-25" @default.
- W2477852672 title "Intracerebral Gene Transfer Using Viral Vectors" @default.
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