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- W2522810014 abstract "Os lentivirus, bem como os oncovirus e os spumavirus, pertencem a familia Retroviridae. Essa familia possui genoma composto por duas fitas simples de RNA e enzima transcriptase reversa. Os virus de imunodeficiencia humana (HIV), felina (FIV) e simiana (SIV) sao os representantes mais bem conhecidos dos lentivirus, devido aos seus efeitos patologicos. O genoma dos lentivirus apresenta uma organizacao mais complexa do que dos oncovirus e muitos dos seus processos moleculares ja estao descritos OU ja sao conhecidos. Alem disso, sao capazes de infectar inclusive celulas quiescentes, caracteristicas essa que se opoe ao tropismo dos oncovirus. Essas propriedades levaram ao desenvolvimento de vetores lentivirais para terapia genica e a perspectiva do emprego terapeutico dos mesmos na clinica – por exemplo, para sindrome da imunodeficiencia adquirida (SIDA). Uma serie de modificacoes de engenharia genetica no lentivetor baseado em HIV levou ao desenvolvimento do primeiro protocolo clinico de terapia genica lentiviral contra a SIDA, nos EUA. Atualmente, existem varios protocolos clinicos com lentivetores em andamento, seguindo a tendencia de emprega-los tambem em outras doencas. Descritores: Lentivetores, terapia genica, vetor viral. SUMMARY" @default.
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- W2522810014 date "2008-01-01" @default.
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- W2522810014 title "The Potentiality of Lentivectors in Gene Therapy" @default.
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