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- W2570298531 endingPage "165" @default.
- W2570298531 startingPage "141" @default.
- W2570298531 abstract "Motor neuron diseases, such as amyotrophic lateral sclerosis (ALS) and spinal muscular atrophy (SMA), are devastating neurodegenerative diseases that are progressive and fatal. There is no cure and the current standard of care is merely palliative. For example, riluzole is the only FDA-approved treatment for ALS and extends life for 3–6 months. Due to the inability of conventional therapies to have an impact on these diseases, research in gene and stem cell therapies have come into focus. Gene and stem cell therapies have the potential to make a significant impact on the treatment of ALS and SMA. For this potential to be realized, the optimal gene therapy vector or stem cell needs to be selected. The various options have their pros and cons, which will be discussed in this chapter. It is necessary to take the time to assess and match the disease with the appropriate therapy." @default.
- W2570298531 created "2017-01-13" @default.
- W2570298531 creator A5029971352 @default.
- W2570298531 date "2017-01-01" @default.
- W2570298531 modified "2023-10-13" @default.
- W2570298531 title "Introduction to Gene and Stem-Cell Therapy" @default.
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