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- W2588272004 abstract "Key Points Only a few F9 nonsense mutations are responsive to drug-induced readthrough due to specific translation and protein structural constraints. Reinsertion of the WT residue and gain-of-function effects account for functionally relevant readthrough." @default.
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- W2588272004 date "2017-04-20" @default.
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- W2588272004 title "Specific factor IX mRNA and protein features favor drug-induced readthrough over recurrent nonsense mutations" @default.
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- W2588272004 doi "https://doi.org/10.1182/blood-2016-09-738641" @default.
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