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- W2596267980 abstract "The use of splice-switching antisense therapy is highly promising, with a wealth of pre-clinical data and numerous clinical trials ongoing. Nevertheless, its potential to treat a variety of disorders has yet to be realized. The main obstacle impeding the clinical translation of this approach is the relatively poor delivery of antisense oligonucleotides to target tissues after systemic delivery. We are a group of researchers closely involved in the development of these therapies and would like to communicate our discussions concerning the validity of standard methodologies currently used in their pre-clinical development, the gaps in current knowledge and the pertinent challenges facing the field. We therefore make recommendations in order to focus future research efforts and facilitate a wider application of therapeutic antisense oligonucleotides." @default.
- W2596267980 created "2017-03-23" @default.
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- W2596267980 date "2017-03-13" @default.
- W2596267980 modified "2023-10-16" @default.
- W2596267980 title "Delivery is key: lessons learnt from developing splice‐switching antisense therapies" @default.
- W2596267980 cites W14741340 @default.
- W2596267980 cites W1502920935 @default.
- W2596267980 cites W1533447420 @default.
- W2596267980 cites W1553529648 @default.
- W2596267980 cites W1643374506 @default.
- W2596267980 cites W166353499 @default.
- W2596267980 cites W1783807361 @default.
- W2596267980 cites W1963958243 @default.
- W2596267980 cites W1967067462 @default.
- W2596267980 cites W1971880391 @default.
- W2596267980 cites W1972841312 @default.
- W2596267980 cites W1977485913 @default.
- W2596267980 cites W1982257974 @default.
- W2596267980 cites W1991945869 @default.
- W2596267980 cites W1996620665 @default.
- W2596267980 cites W1997327853 @default.
- W2596267980 cites W1997730532 @default.
- W2596267980 cites W2000055548 @default.
- W2596267980 cites W2004909530 @default.
- W2596267980 cites W2005245653 @default.
- W2596267980 cites W2012894204 @default.
- W2596267980 cites W2017885537 @default.
- W2596267980 cites W2024858641 @default.
- W2596267980 cites W2029126306 @default.
- W2596267980 cites W2030120319 @default.
- W2596267980 cites W2030234137 @default.
- W2596267980 cites W2033179276 @default.
- W2596267980 cites W2033425827 @default.
- W2596267980 cites W2037695327 @default.
- W2596267980 cites W2038428739 @default.
- W2596267980 cites W2039901723 @default.
- W2596267980 cites W2042915950 @default.
- W2596267980 cites W2048594170 @default.
- W2596267980 cites W2054032118 @default.
- W2596267980 cites W2062078686 @default.
- W2596267980 cites W2064761355 @default.
- W2596267980 cites W2065603844 @default.
- W2596267980 cites W2074766632 @default.
- W2596267980 cites W2077301034 @default.
- W2596267980 cites W2078163685 @default.
- W2596267980 cites W2082175825 @default.
- W2596267980 cites W2083266053 @default.
- W2596267980 cites W2088060365 @default.
- W2596267980 cites W2088707712 @default.
- W2596267980 cites W2090804804 @default.
- W2596267980 cites W2090849645 @default.
- W2596267980 cites W2092006545 @default.
- W2596267980 cites W2093555758 @default.
- W2596267980 cites W2100279229 @default.
- W2596267980 cites W2110934178 @default.
- W2596267980 cites W2114051020 @default.
- W2596267980 cites W2114609224 @default.
- W2596267980 cites W2114775015 @default.
- W2596267980 cites W2117224856 @default.
- W2596267980 cites W2118601234 @default.
- W2596267980 cites W2127310182 @default.
- W2596267980 cites W2128768698 @default.
- W2596267980 cites W2133696920 @default.
- W2596267980 cites W2134753663 @default.
- W2596267980 cites W2140534435 @default.
- W2596267980 cites W2143743183 @default.
- W2596267980 cites W2147842670 @default.
- W2596267980 cites W2151448282 @default.
- W2596267980 cites W2152060821 @default.
- W2596267980 cites W2153940274 @default.
- W2596267980 cites W2155239981 @default.
- W2596267980 cites W2157365614 @default.
- W2596267980 cites W2157979200 @default.
- W2596267980 cites W2158041351 @default.
- W2596267980 cites W2162372723 @default.
- W2596267980 cites W2164779038 @default.
- W2596267980 cites W2168862406 @default.
- W2596267980 cites W2171776498 @default.
- W2596267980 cites W2172085519 @default.
- W2596267980 cites W2174292614 @default.