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- W2743746405 abstract "In a patient induced pluripotent stem cell model of the hereditary dilated cardiomyopathy caused by a frameshift mutation in titin exon 326, we show beneficial effects of reframing titin mRNA by exon skipping, suggesting a potential therapy for the disease. Moreover, we established optical action potential recordings in specific hiPSC-CM subtypes as a precise and high-throughput system for disease modelling and drug evaluation in the relevant cells types." @default.
- W2743746405 created "2017-08-17" @default.
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- W2743746405 date "2016-01-01" @default.
- W2743746405 modified "2023-09-26" @default.
- W2743746405 title "Human iPSC-derived cardiomyocytes as platforms for cardiac disease modeling, therapeutic discovery and safety pharmacology" @default.
- W2743746405 hasPublicationYear "2016" @default.
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