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- W2756992211 abstract "Genome editing using clustered regularly interspersed short palindromic repeats (CRISPR) and CRISPR-associated proteins offers the potential to facilitate safe and effective treatment of genetic diseases refractory to other types of intervention. Here, we identify some of the major challenges for clinicians, regulators, and human research ethics committees in the clinical translation of CRISPR-mediated somatic cell therapy." @default.
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- W2756992211 date "2017-09-25" @default.
- W2756992211 modified "2023-09-28" @default.
- W2756992211 title "Key challenges in bringing CRISPR-mediated somatic cell therapy into the clinic" @default.
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- W2756992211 doi "https://doi.org/10.1186/s13073-017-0475-4" @default.
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