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- W2765682724 abstract "A 55-year-old man was admitted to our institute to undergo evaluation for proteinuria (5.4 g/day) with lambda-type Bence-Jones protein (BJP). Primary amyloid light chain (AL) amyloidosis and acquired factor X deficiency were diagnosed. High-dose melphalan combined with autologous stem cell transplantation was performed. After three years, the patient's proteinuria normalized, he was negative for urinary BJP, and his factor X activity improved to 105%. Serial renal biopsy showed no progression of amyloid deposition at a biopsy after 5 years, but showed a slight increase in the amyloid deposition after 11 years. This therapy can improve the prognosis of AL amyloidosis; however, there are limitations to the strategy." @default.
- W2765682724 created "2017-11-10" @default.
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- W2765682724 date "2018-01-01" @default.
- W2765682724 modified "2023-10-16" @default.
- W2765682724 title "The Long-term Outcomes after VAD plus SCT Therapy in a Patient with AL Amyloidosis and Severe Factor X Deficiency" @default.
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- W2765682724 doi "https://doi.org/10.2169/internalmedicine.9263-17" @default.
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