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- W2766376439 endingPage "394" @default.
- W2766376439 startingPage "382" @default.
- W2766376439 abstract "There are tremendous unmet needs in drug development for rare diseases. Computational drug repositioning is a promising approach and has been successfully applied to the development of treatments for diseases. However, how to utilize this knowledge and effectively conduct and implement computational drug repositioning approaches for rare disease therapies is still an open issue. Here, we focus on the means of utilizing accumulated genomic data for accelerating and facilitating drug repositioning for rare diseases. First, we summarize the current genome landscape of rare diseases. Second, we propose several promising bioinformatics approaches and pipelines for computational drug repositioning for rare diseases. Finally, we discuss recent regulatory incentives and other enablers in rare disease drug development and outline the remaining challenges." @default.
- W2766376439 created "2017-11-10" @default.
- W2766376439 creator A5004812494 @default.
- W2766376439 creator A5011366541 @default.
- W2766376439 creator A5046722857 @default.
- W2766376439 creator A5068886380 @default.
- W2766376439 creator A5086234334 @default.
- W2766376439 creator A5089640396 @default.
- W2766376439 date "2018-02-01" @default.
- W2766376439 modified "2023-10-16" @default.
- W2766376439 title "Computational drug repositioning for rare diseases in the era of precision medicine" @default.
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