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- W2767910004 endingPage "137" @default.
- W2767910004 startingPage "119" @default.
- W2767910004 abstract "Gene therapy refers to the use of viral and nonviral vectors to deliver nucleic acids to target tissues. First employed to replace defective genes in monogenetic diseases, such as inborn errors of metabolism and blood disorders, gene therapy has more recently been adopted to express transgenes at sites of injury to promote or facilitate repair. In this chapter, we focus on recent achievements in gene therapy for inherited and acquired disorders of and injuries to connective tissues, such as bone, cartilage, and tendon. The basic principles of in vivo and ex vivo gene therapy will be described. Furthermore, an overview will be given of the viral and nonviral vectors used in the field and their associated immunological concerns. A number of skeletal disorders and injury types that have been treated using gene therapy will be discussed, including candidate genes and approaches. Finally, an outlook for the future of gene therapy for skeletal pathologies will be given." @default.
- W2767910004 created "2017-11-17" @default.
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- W2767910004 creator A5076988359 @default.
- W2767910004 creator A5089856478 @default.
- W2767910004 date "2018-01-01" @default.
- W2767910004 modified "2023-09-24" @default.
- W2767910004 title "Prospects of Gene Therapy for Skeletal Diseases" @default.
- W2767910004 cites W105600474 @default.
- W2767910004 cites W1269576713 @default.
- W2767910004 cites W143584679 @default.
- W2767910004 cites W1459572188 @default.
- W2767910004 cites W1481225665 @default.
- W2767910004 cites W1489362484 @default.
- W2767910004 cites W1491727665 @default.
- W2767910004 cites W1515122536 @default.
- W2767910004 cites W1521151957 @default.
- W2767910004 cites W1529674879 @default.
- W2767910004 cites W1573020176 @default.
- W2767910004 cites W1581844310 @default.
- W2767910004 cites W1586872180 @default.
- W2767910004 cites W1779098814 @default.
- W2767910004 cites W1790927147 @default.
- W2767910004 cites W1793778442 @default.
- W2767910004 cites W1861255861 @default.
- W2767910004 cites W1865442119 @default.
- W2767910004 cites W1890735177 @default.
- W2767910004 cites W1891210761 @default.
- W2767910004 cites W1897577213 @default.
- W2767910004 cites W1916449534 @default.
- W2767910004 cites W192917232 @default.
- W2767910004 cites W1963698651 @default.
- W2767910004 cites W1965029377 @default.
- W2767910004 cites W1965040938 @default.
- W2767910004 cites W1965631524 @default.
- W2767910004 cites W1966185500 @default.
- W2767910004 cites W1968006472 @default.
- W2767910004 cites W1969834555 @default.
- W2767910004 cites W1970285081 @default.
- W2767910004 cites W1970419845 @default.
- W2767910004 cites W1973284822 @default.
- W2767910004 cites W1976300747 @default.
- W2767910004 cites W1980822790 @default.
- W2767910004 cites W1982712041 @default.
- W2767910004 cites W1985148995 @default.
- W2767910004 cites W1985716862 @default.
- W2767910004 cites W1986290362 @default.
- W2767910004 cites W1987138690 @default.
- W2767910004 cites W1987412932 @default.
- W2767910004 cites W1987480613 @default.
- W2767910004 cites W1989174295 @default.
- W2767910004 cites W1989500669 @default.
- W2767910004 cites W1990338062 @default.
- W2767910004 cites W1992001457 @default.
- W2767910004 cites W1994390268 @default.
- W2767910004 cites W1994495694 @default.
- W2767910004 cites W1996530389 @default.
- W2767910004 cites W1998302327 @default.
- W2767910004 cites W1999747962 @default.
- W2767910004 cites W1999971801 @default.
- W2767910004 cites W2000465858 @default.
- W2767910004 cites W2000973590 @default.
- W2767910004 cites W2001243226 @default.
- W2767910004 cites W2001644736 @default.
- W2767910004 cites W2001723304 @default.
- W2767910004 cites W2002535790 @default.
- W2767910004 cites W2005044790 @default.
- W2767910004 cites W2008351901 @default.
- W2767910004 cites W2008477183 @default.
- W2767910004 cites W2010797042 @default.
- W2767910004 cites W2013384673 @default.
- W2767910004 cites W2014549124 @default.
- W2767910004 cites W2015404892 @default.
- W2767910004 cites W2017458997 @default.
- W2767910004 cites W2019196925 @default.
- W2767910004 cites W2021988589 @default.
- W2767910004 cites W2022429082 @default.
- W2767910004 cites W2024135486 @default.
- W2767910004 cites W2025760764 @default.
- W2767910004 cites W2027583787 @default.
- W2767910004 cites W2028153000 @default.
- W2767910004 cites W2028591598 @default.
- W2767910004 cites W2028792773 @default.
- W2767910004 cites W2029336962 @default.
- W2767910004 cites W2032678451 @default.
- W2767910004 cites W2034640715 @default.
- W2767910004 cites W2036127017 @default.
- W2767910004 cites W2039114465 @default.
- W2767910004 cites W2040528896 @default.
- W2767910004 cites W2041368501 @default.
- W2767910004 cites W2042234246 @default.
- W2767910004 cites W2042496269 @default.
- W2767910004 cites W2042712894 @default.
- W2767910004 cites W2046488302 @default.
- W2767910004 cites W2047689196 @default.
- W2767910004 cites W2049799550 @default.