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- W2773253161 abstract "The prevention of bleeding with adequately sustained levels of clotting factor, after a single therapeutic intervention and without the need for further medical intervention, represents an important goal in the treatment of hemophilia." @default.
- W2773253161 created "2017-12-22" @default.
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- W2773253161 date "2017-12-07" @default.
- W2773253161 modified "2023-10-17" @default.
- W2773253161 title "Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant" @default.
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- W2773253161 doi "https://doi.org/10.1056/nejmoa1708538" @default.
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