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- W2775976710 abstract "A shot of DNA-filled viruses injected directly into the eye is now the first gene therapy approved by the U.S. Food & Drug Administration to treat a genetic disease. The therapy, called Luxturna, was developed by Philadelphia-based Spark Therapeutics and treats a form of inherited blindness. “I believe gene therapy will become a mainstay in treating, and maybe curing, many of our most devastating and intractable illnesses,” FDA Commissioner Scott Gottlieb said. “We’re at a turning point when it comes to this novel form of therapy.” During a press briefing, Gottlieb heralded Luxturna as FDA’s third gene therapy approval in 2017. The first two were CAR T-cell immunotherapies, in which a patient’s immune cells are removed, injected with DNA outside the body, and returned to the bloodstream to fight cancer cells. Luxturna, though, is the first treatment that fits the traditional notion of gene therapy, whereby DNA-filled viruses are injected" @default.
- W2775976710 created "2018-01-05" @default.
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- W2775976710 date "2018-01-01" @default.
- W2775976710 modified "2023-10-16" @default.
- W2775976710 title "First gene therapy for genetic disease approved" @default.
- W2775976710 doi "https://doi.org/10.1021/cen-09601-notw11" @default.
- W2775976710 hasPublicationYear "2018" @default.
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