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- W2891574963 abstract "Over the last decade, cyclodextrins (CDs) have gained considerable attention as a potential therapeutic intervention in the treatment of the rare genetic condition Niemann-Pick type C disease (NPC). However, the oligosaccharide in its monomeric form suffers from serious side effects, especially from a pharmacokinetic and biodistribution standpoint. CD-based macromolecular systems hold great promise to overcome such limitations and might provide an improved therapeutic approach in reducing cholesterol accumulation in NPC. In the present article, the latest developments and synthetic strategies in the preparation of CD-containing polymers as cholesterol-mopping therapeutic agents in NPC are summarized." @default.
- W2891574963 created "2018-09-27" @default.
- W2891574963 creator A5018094815 @default.
- W2891574963 creator A5023158705 @default.
- W2891574963 date "2018-09-14" @default.
- W2891574963 modified "2023-10-17" @default.
- W2891574963 title "Cyclodextrin-Based Macromolecular Systems as Cholesterol-Mopping Therapeutic Agents in Niemann-Pick Disease Type C" @default.
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- W2891574963 doi "https://doi.org/10.1002/marc.201800557" @default.
- W2891574963 hasPubMedId "https://pubmed.ncbi.nlm.nih.gov/30216584" @default.