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- W2895037149 abstract "Summary Targeting genes to specific neuronal or glial cell types is valuable both for understanding and for repairing brain circuits. Adeno-associated viral vectors (AAVs) are frequently used for gene delivery, but targeting expression to specific cell types is a challenge. We created a library of 230 AAVs, each with a different synthetic promoter designed using four independent strategies. We show that ~11% of these AAVs specifically target expression to neuronal and glial cell types in the mouse retina, mouse brain, non-human primate retina in vivo , and in the human retina in vitro . We demonstrate applications for recording, stimulation, and molecular characterization, as well as the intersectional and combinatorial labeling of cell types. These resources and approaches allow economic, fast, and efficient cell-type targeting in a variety of species, both for fundamental science and for gene therapy." @default.
- W2895037149 created "2018-10-12" @default.
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- W2895037149 date "2018-10-04" @default.
- W2895037149 modified "2023-10-14" @default.
- W2895037149 title "Targeting neuronal and glial cell types with synthetic promoter AAVs in mice, non-human primates, and humans" @default.
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- W2895037149 doi "https://doi.org/10.1101/434720" @default.
- W2895037149 hasPublicationYear "2018" @default.
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