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- W2897626245 abstract "VX-445 is a next-generation cystic fibrosis transmembrane conductance regulator (CFTR) corrector designed to restore Phe508del CFTR protein function in patients with cystic fibrosis when administered with tezacaftor and ivacaftor (VX-445–tezacaftor–ivacaftor)." @default.
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- W2897626245 date "2018-10-25" @default.
- W2897626245 modified "2023-10-18" @default.
- W2897626245 title "VX-445–Tezacaftor–Ivacaftor in Patients with Cystic Fibrosis and One or Two Phe508del Alleles" @default.
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- W2897626245 doi "https://doi.org/10.1056/nejmoa1807120" @default.
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