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- W2906240214 endingPage "31" @default.
- W2906240214 startingPage "23" @default.
- W2906240214 abstract "Cystic fibrosis is a monogenic autosomal recessive disorder caused by mutations in CFTR gene. Until recent days, cystic fibrosis therapy was limited to symptomatic treatment of respiratory infections and malabsorption. In last years pathogenetic therapy of the disease received significant progress and premises for development of new methods of gene therapy came into sight. In the review, modern methods of cystic fibrosis treatment are considered, some of them are already used in the clinic (pathogenesis-based therapy with CFTR modulators), while the other part is only developing (gene therapy, including genome editing and cell therapy)." @default.
- W2906240214 created "2019-01-01" @default.
- W2906240214 creator A5054376895 @default.
- W2906240214 creator A5060546352 @default.
- W2906240214 date "2018-09-15" @default.
- W2906240214 modified "2023-10-18" @default.
- W2906240214 title "Modern pathogenesis-based methods and development of new gene and cell-based methods for cystic fibrosis treatment" @default.
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- W2906240214 doi "https://doi.org/10.23868/201811029" @default.
- W2906240214 hasPublicationYear "2018" @default.
- W2906240214 type Work @default.