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- W2991380003 endingPage "1091" @default.
- W2991380003 startingPage "1091" @default.
- W2991380003 abstract "Foamy viruses (FVs) are nonpathogenic retroviruses that infect various animals including bovines, felines, nonhuman primates (NHPs), and can be transmitted to humans through zoonotic infection. Due to their non-pathogenic nature, broad tissue tropism and relatively safe integration profile, FVs have been engineered as novel vectors (foamy virus vector, FVV) for stable gene transfer into different cells and tissues. FVVs have emerged as an alternative platform to contemporary viral vectors (e.g., adeno associated and lentiviral vectors) for experimental and therapeutic gene therapy of a variety of monogenetic diseases. Some of the important features of FVVs include the ability to efficiently transduce hematopoietic stem and progenitor cells (HSPCs) from humans, NHPs, canines and rodents. We have successfully used FVV for proof of concept studies to demonstrate safety and efficacy following in-vivo delivery in large animal models. In this review, we will comprehensively discuss FVV based in-vivo gene therapy approaches established in the X-linked severe combined immunodeficiency (SCID-X1) canine model." @default.
- W2991380003 created "2019-12-05" @default.
- W2991380003 creator A5038095922 @default.
- W2991380003 creator A5060993908 @default.
- W2991380003 creator A5081792956 @default.
- W2991380003 date "2019-11-23" @default.
- W2991380003 modified "2023-10-03" @default.
- W2991380003 title "In-Vivo Gene Therapy with Foamy Virus Vectors" @default.
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