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- W3019585265 endingPage "309" @default.
- W3019585265 startingPage "299" @default.
- W3019585265 abstract "Epidermolysis bullosa (EB) is a group of rare genetic disorders for which significant progress has been achieved in the development of molecular therapies in the last few decades. Such therapies require knowledge of mutant genes and specific mutations, some of them being allele specific. A relatively large number of clinical trials are ongoing and ascertaining the clinical efficacy of gene, protein or cell therapies or of repurposed drugs, mainly in recessive dystrophic EB. It is expected that some new drugs may emerge in the near future and that combinations of different approaches may result in improved treatment outcomes for individuals with EB." @default.
- W3019585265 created "2020-05-01" @default.
- W3019585265 creator A5032533037 @default.
- W3019585265 creator A5058074251 @default.
- W3019585265 creator A5088114081 @default.
- W3019585265 date "2020-04-23" @default.
- W3019585265 modified "2023-10-16" @default.
- W3019585265 title "Molecular Therapeutics in Development for Epidermolysis Bullosa: Update 2020" @default.
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