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- W3033754923 endingPage "83" @default.
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- W3033754923 abstract "Abstract The fact that monogenic diseases are related to mutations in one specific gene, make gene correction one of the promising strategies in the future to treat genetic diseases or alleviate their symptoms. From this perspective, and along with recent advances in technology, genome editing tools have gained momentum and developed fast. In fact, clustered regularly interspaced short palindromic repeats‐associated protein 9 (CRISPR/Cas9), transcription activator‐like effector nucleases (TALENs), and zinc‐finger nucleases (ZFNs) are regarded as novel technologies which are able to correct a number of genetic aberrations in vitro and in vivo. The number of ongoing clinical trials employing these tools has been increased showing the encouraging outcomes of these tools. However, there are still some major challenges with respect to the safety profile and directed delivery of them. In this paper, we provided updated information regarding the history, nature, methods of delivery, and application of the above‐mentioned gene editing tools along with the meganucleases (an older similar tool) based on published in vitro and in vivo studies and introduced clinical trials which employed these technologies." @default.
- W3033754923 created "2020-06-12" @default.
- W3033754923 creator A5002693195 @default.
- W3033754923 creator A5026614780 @default.
- W3033754923 creator A5033593212 @default.
- W3033754923 creator A5058516379 @default.
- W3033754923 creator A5060001313 @default.
- W3033754923 creator A5067115754 @default.
- W3033754923 creator A5069750662 @default.
- W3033754923 creator A5075005577 @default.
- W3033754923 date "2020-08-24" @default.
- W3033754923 modified "2023-10-18" @default.
- W3033754923 title "Gene editing technology for improving life quality: A dream coming true?" @default.
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