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- W30358587 abstract "Successful bone marrow transplantation (BMT) for treating genetic diseases in animals and man was first performed in the late 1960s. (1967) corrected hereditary spherocytosis in an animal, closely followed by successful treatment of boys with severe combined immunodeficiency (SCID) (Gatti et al., 1968). The relative absence of T-cell function in the SCID patients allowed engraftment without chemotherapy to prevent immune rejection. However, it soon became apparent that only a limited number of diseases (all of them immunodeficiency states) could be treated so simply, and work began to develop effective chemotherapy conditioning regimes.KeywordsChronic Granulomatous DiseaseGraft Versus Host DiseaseFanconi AnemiaAllogeneic Bone Marrow TransplantationMetachromatic LeukodystrophyThese keywords were added by machine and not by the authors. This process is experimental and the keywords may be updated as the learning algorithm improves." @default.
- W30358587 created "2016-06-24" @default.
- W30358587 creator A5030646889 @default.
- W30358587 date "1999-01-01" @default.
- W30358587 modified "2023-09-27" @default.
- W30358587 title "Bone Marrow Transplantation for Genetic Diseases" @default.
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