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- W3048418602 endingPage "759" @default.
- W3048418602 startingPage "759" @default.
- W3048418602 abstract "DNA delivery is at the forefront of current research efforts in gene therapy and synthetic biology. Viral vectors have traditionally dominated the field; however, nonviral delivery systems are increasingly gaining traction. Baculoviruses are arthropod-specific viruses that can be easily engineered and repurposed to accommodate and deliver large sequences of exogenous DNA into mammalian cells, tissues, or ultimately organisms. These synthetic virus-derived nanosystems (SVNs) are safe, readily customized, and can be manufactured at scale. By implementing clustered regularly interspaced palindromic repeats (CRISPR) associated protein (CRISPR/Cas) modalities into this system, we developed SVNs capable of inserting complex DNAs into genomes, at base pair precision. We anticipate a major role for SVNs as an attractive alternative to viral vectors in accelerating genome engineering and gene therapy applications in the future." @default.
- W3048418602 created "2020-08-18" @default.
- W3048418602 creator A5013136404 @default.
- W3048418602 creator A5071010818 @default.
- W3048418602 creator A5091178241 @default.
- W3048418602 date "2020-08-11" @default.
- W3048418602 modified "2023-09-30" @default.
- W3048418602 title "Synthetic Virus-Derived Nanosystems (SVNs) for Delivery and Precision Docking of Large Multifunctional DNA Circuitry in Mammalian Cells" @default.
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- W3048418602 doi "https://doi.org/10.3390/pharmaceutics12080759" @default.
- W3048418602 hasPubMedCentralId "https://www.ncbi.nlm.nih.gov/pmc/articles/7466058" @default.