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- W3088696501 endingPage "1113" @default.
- W3088696501 startingPage "1113" @default.
- W3088696501 abstract "Impressive therapeutic advances have been possible through the advent of zinc-finger nucleases and transcription activator-like effector nucleases. However, discovery of the more efficient and highly tailorable clustered regularly interspaced short palindromic repeats (CRISPR) and associated proteins (Cas9) has provided unprecedented gene-editing capabilities for treatment of various inherited and acquired diseases. Despite recent clinical trials, a major barrier for therapeutic gene editing is the absence of safe and effective methods for local and systemic delivery of gene-editing reagents. In this review, we elaborate on the challenges and provide practical considerations for improving gene editing. Specifically, we highlight issues associated with delivery of gene-editing tools into clinically relevant cells." @default.
- W3088696501 created "2020-10-01" @default.
- W3088696501 creator A5009449947 @default.
- W3088696501 creator A5011400475 @default.
- W3088696501 creator A5024968635 @default.
- W3088696501 creator A5070873889 @default.
- W3088696501 creator A5073882029 @default.
- W3088696501 date "2020-09-23" @default.
- W3088696501 modified "2023-10-01" @default.
- W3088696501 title "Delivery Approaches for Therapeutic Genome Editing and Challenges" @default.
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