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- W3093469725 endingPage "859" @default.
- W3093469725 startingPage "839" @default.
- W3093469725 abstract "Base editing - the introduction of single-nucleotide variants (SNVs) into DNA or RNA in living cells - is one of the most recent advances in the field of genome editing. As around half of known pathogenic genetic variants are due to SNVs, base editing holds great potential for the treatment of numerous genetic diseases, through either temporary RNA or permanent DNA base alterations. Recent advances in the specificity, efficiency, precision and delivery of DNA and RNA base editors are revealing exciting therapeutic opportunities for these technologies. We expect the correction of single point mutations will be a major focus of future precision medicine." @default.
- W3093469725 created "2020-10-22" @default.
- W3093469725 creator A5039558005 @default.
- W3093469725 creator A5044327001 @default.
- W3093469725 creator A5076502944 @default.
- W3093469725 creator A5082310752 @default.
- W3093469725 date "2020-10-19" @default.
- W3093469725 modified "2023-10-17" @default.
- W3093469725 title "Base editing: advances and therapeutic opportunities" @default.
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