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- W3134729462 abstract "Abstract Three recent approvals and over 100 ongoing clinical trials make adeno‐associated virus (AAV)‐based vectors the leading gene delivery vehicles in gene therapy. Pharmaceutical companies are investing in this small and nonpathogenic gene shuttle to increase the therapeutic portfolios within the coming years. This prospect of marking a new era in gene therapy has fostered both investigations of the fundamental AAV biology as well as engineering studies to enhance delivery vehicles. Driven by the high clinical potential, a new generation of synthetic‐biologically engineered AAV vectors is on the rise. Concepts from synthetic biology enable the control and fine‐tuning of vector function at different stages of cellular transduction and gene expression. It is anticipated that the emerging field of synthetic‐biologically engineered AAV vectors can shape future gene therapeutic approaches and thus the design of tomorrow's gene delivery vectors. This review describes and discusses the recent trends in capsid and vector genome engineering, with particular emphasis on synthetic‐biological approaches." @default.
- W3134729462 created "2021-03-15" @default.
- W3134729462 creator A5082252506 @default.
- W3134729462 creator A5084630304 @default.
- W3134729462 creator A5089723990 @default.
- W3134729462 date "2021-02-26" @default.
- W3134729462 modified "2023-10-06" @default.
- W3134729462 title "Synthetic Biology: Emerging Concepts to Design and Advance Adeno‐Associated Viral Vectors for Gene Therapy" @default.
- W3134729462 cites W1505196125 @default.
- W3134729462 cites W1518729035 @default.
- W3134729462 cites W1541189153 @default.
- W3134729462 cites W1598111769 @default.
- W3134729462 cites W1607008970 @default.
- W3134729462 cites W1619761819 @default.
- W3134729462 cites W1755517856 @default.
- W3134729462 cites W1857324335 @default.
- W3134729462 cites W1963143659 @default.
- W3134729462 cites W1963788023 @default.
- W3134729462 cites W1964959966 @default.
- W3134729462 cites W1966850918 @default.
- W3134729462 cites W1967663075 @default.
- W3134729462 cites W1969538192 @default.
- W3134729462 cites W1970586355 @default.
- W3134729462 cites W1972318514 @default.
- W3134729462 cites W1973733861 @default.
- W3134729462 cites W1975048313 @default.
- W3134729462 cites W1981130347 @default.
- W3134729462 cites W1983332324 @default.
- W3134729462 cites W1984922546 @default.
- W3134729462 cites W1985889861 @default.
- W3134729462 cites W1987005832 @default.
- W3134729462 cites W1988156814 @default.
- W3134729462 cites W1989429684 @default.
- W3134729462 cites W1990077703 @default.
- W3134729462 cites W1990622714 @default.
- W3134729462 cites W1990842598 @default.
- W3134729462 cites W1990952318 @default.
- W3134729462 cites W1992275565 @default.
- W3134729462 cites W1993018547 @default.
- W3134729462 cites W1994710975 @default.
- W3134729462 cites W1995854207 @default.
- W3134729462 cites W1999625705 @default.
- W3134729462 cites W2001444550 @default.
- W3134729462 cites W2001831734 @default.
- W3134729462 cites W2001999470 @default.
- W3134729462 cites W2003885556 @default.
- W3134729462 cites W2005291427 @default.
- W3134729462 cites W2005334224 @default.
- W3134729462 cites W2005389545 @default.
- W3134729462 cites W2006920577 @default.
- W3134729462 cites W2007187950 @default.
- W3134729462 cites W2008033906 @default.
- W3134729462 cites W2008342629 @default.
- W3134729462 cites W2009247311 @default.
- W3134729462 cites W2009681413 @default.
- W3134729462 cites W2009792531 @default.
- W3134729462 cites W2010388612 @default.
- W3134729462 cites W2010666698 @default.
- W3134729462 cites W2010872781 @default.
- W3134729462 cites W2011742128 @default.
- W3134729462 cites W2012034410 @default.
- W3134729462 cites W2012530297 @default.
- W3134729462 cites W2016364569 @default.
- W3134729462 cites W2017456159 @default.
- W3134729462 cites W2017969617 @default.
- W3134729462 cites W2018665497 @default.
- W3134729462 cites W2020652110 @default.
- W3134729462 cites W2022031776 @default.
- W3134729462 cites W2023687851 @default.
- W3134729462 cites W2025579609 @default.
- W3134729462 cites W2025725192 @default.
- W3134729462 cites W2027634316 @default.
- W3134729462 cites W2029852810 @default.
- W3134729462 cites W2031675363 @default.
- W3134729462 cites W2032218738 @default.
- W3134729462 cites W2033535780 @default.
- W3134729462 cites W2033630555 @default.
- W3134729462 cites W2035052089 @default.
- W3134729462 cites W2035758624 @default.
- W3134729462 cites W2036600728 @default.
- W3134729462 cites W2037735567 @default.
- W3134729462 cites W2037962246 @default.
- W3134729462 cites W2039583977 @default.
- W3134729462 cites W2040516865 @default.
- W3134729462 cites W2041961234 @default.
- W3134729462 cites W2044597443 @default.
- W3134729462 cites W2045490787 @default.
- W3134729462 cites W2047667011 @default.
- W3134729462 cites W2048162805 @default.
- W3134729462 cites W2048651210 @default.
- W3134729462 cites W2049134806 @default.
- W3134729462 cites W2049345986 @default.
- W3134729462 cites W2049558117 @default.
- W3134729462 cites W2050754173 @default.
- W3134729462 cites W2051047653 @default.
- W3134729462 cites W2051072233 @default.
- W3134729462 cites W2054677438 @default.
- W3134729462 cites W2061013034 @default.
- W3134729462 cites W2064736759 @default.
- W3134729462 cites W2066015597 @default.