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- W3177377165 abstract "Duchenne muscular dystrophy is a genetic disorder where an X-linked mutation in the DMD gene initiates pathogenic development caused by the absence of dystrophin protein. This impacts primarily the evolution of a functional muscle tissue resulting in muscle weakness and later severe disability in young male patients leading to an early death. Patients in the final stage develop dilated cardiomyopathy leading ultimately to cardiac or respiratory failure as the cause of death. This review discusses recent advances in modeling the DMD pathology in vitro. It describes in detail the molecular abnormalities found on the cellular and organoid levels. The in vitro pathology is compared to that found in patients. Likewise, the drawbacks and limitations of current models are discussed." @default.
- W3177377165 created "2021-07-05" @default.
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- W3177377165 creator A5074680508 @default.
- W3177377165 date "2021-06-24" @default.
- W3177377165 modified "2023-10-18" @default.
- W3177377165 title "Cellular pathology of the human heart in Duchenne muscular dystrophy (DMD): lessons learned from in vitro modeling" @default.
- W3177377165 cites W1422903567 @default.
- W3177377165 cites W1429841006 @default.
- W3177377165 cites W1533055515 @default.
- W3177377165 cites W1747672433 @default.
- W3177377165 cites W1756023647 @default.
- W3177377165 cites W1850477203 @default.
- W3177377165 cites W1905132822 @default.
- W3177377165 cites W1942450988 @default.
- W3177377165 cites W1952000723 @default.
- W3177377165 cites W1971143219 @default.
- W3177377165 cites W1973189339 @default.
- W3177377165 cites W1979992454 @default.
- W3177377165 cites W1986088843 @default.
- W3177377165 cites W1986950000 @default.
- W3177377165 cites W1989113874 @default.
- W3177377165 cites W1990433203 @default.
- W3177377165 cites W1990897270 @default.
- W3177377165 cites W1995347512 @default.
- W3177377165 cites W1995621893 @default.
- W3177377165 cites W2002564042 @default.
- W3177377165 cites W2002588694 @default.
- W3177377165 cites W2009324880 @default.
- W3177377165 cites W2010368308 @default.
- W3177377165 cites W2012208277 @default.
- W3177377165 cites W2017883346 @default.
- W3177377165 cites W2018753432 @default.
- W3177377165 cites W2020685420 @default.
- W3177377165 cites W2023394535 @default.
- W3177377165 cites W2033676880 @default.
- W3177377165 cites W2034421608 @default.
- W3177377165 cites W2037216224 @default.
- W3177377165 cites W2043658665 @default.
- W3177377165 cites W2046027917 @default.
- W3177377165 cites W2046329168 @default.
- W3177377165 cites W2047015778 @default.
- W3177377165 cites W2048658426 @default.
- W3177377165 cites W2052928078 @default.
- W3177377165 cites W2055809007 @default.
- W3177377165 cites W2059155059 @default.
- W3177377165 cites W2062541458 @default.
- W3177377165 cites W2067009965 @default.
- W3177377165 cites W2067067950 @default.
- W3177377165 cites W2068264262 @default.
- W3177377165 cites W2071815825 @default.
- W3177377165 cites W2073047355 @default.
- W3177377165 cites W2080582887 @default.
- W3177377165 cites W2081011369 @default.
- W3177377165 cites W2083599207 @default.
- W3177377165 cites W2087803244 @default.
- W3177377165 cites W2088022023 @default.
- W3177377165 cites W2090663259 @default.
- W3177377165 cites W2092411055 @default.
- W3177377165 cites W2096286415 @default.
- W3177377165 cites W2097136884 @default.
- W3177377165 cites W2098016509 @default.
- W3177377165 cites W2098941422 @default.
- W3177377165 cites W2100250587 @default.
- W3177377165 cites W2101379702 @default.
- W3177377165 cites W2102807861 @default.
- W3177377165 cites W2104790299 @default.
- W3177377165 cites W2106111979 @default.
- W3177377165 cites W2106854179 @default.
- W3177377165 cites W2107138120 @default.
- W3177377165 cites W2107867413 @default.
- W3177377165 cites W2108083474 @default.
- W3177377165 cites W2112943033 @default.
- W3177377165 cites W2118553906 @default.
- W3177377165 cites W2120307618 @default.
- W3177377165 cites W2122902308 @default.
- W3177377165 cites W2126068134 @default.
- W3177377165 cites W2126147950 @default.
- W3177377165 cites W2135793566 @default.
- W3177377165 cites W2137484480 @default.
- W3177377165 cites W2137703332 @default.
- W3177377165 cites W2137714739 @default.
- W3177377165 cites W2141251416 @default.
- W3177377165 cites W2142948622 @default.
- W3177377165 cites W2147048032 @default.
- W3177377165 cites W2154401461 @default.
- W3177377165 cites W2156990620 @default.
- W3177377165 cites W2157112460 @default.
- W3177377165 cites W2157630514 @default.
- W3177377165 cites W2158714558 @default.
- W3177377165 cites W2160943929 @default.
- W3177377165 cites W2164481873 @default.
- W3177377165 cites W2165726438 @default.