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- W3207908423 endingPage "2681" @default.
- W3207908423 startingPage "2681" @default.
- W3207908423 abstract "Metabolic disorders are very common in the population worldwide and are among the diseases with the highest health utilization and costs per person. Despite the ongoing efforts to develop new treatments, currently, for many of these disorders, there are no approved therapies, resulting in a huge economic hit and tension for society. In this review, we recapitulate the recent advancements in stem cell (gene) therapy as potential tools for the long-term treatment of both inherited (lysosomal storage diseases) and acquired (diabetes mellitus, obesity) metabolic disorders, focusing on the main promising results observed in human patients and discussing the critical hurdles preventing the definitive jump of this approach from the bench to the clinic." @default.
- W3207908423 created "2021-10-25" @default.
- W3207908423 creator A5054549234 @default.
- W3207908423 creator A5069394115 @default.
- W3207908423 date "2021-10-07" @default.
- W3207908423 modified "2023-09-26" @default.
- W3207908423 title "Stem Cell Research Tools in Human Metabolic Disorders: An Overview" @default.
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