Matches in SemOpenAlex for { <https://semopenalex.org/work/W3216383239> ?p ?o ?g. }
- W3216383239 endingPage "83" @default.
- W3216383239 startingPage "70" @default.
- W3216383239 abstract "The primary etiology of a diverse range of cardiomyopathies is now understood to be genetic, creating a new paradigm for targeting treatments on the basis of the underlying molecular cause. This review provides a genetic and etiologic context for the traditional clinical classifications of cardiomyopathy, including molecular subtypes that may exhibit differential responses to existing or emerging treatments. The authors describe several emerging cardiomyopathy treatments, including gene therapy, direct targeting of myofilament function, protein quality control, metabolism, and others. The authors discuss advantages and disadvantages of these approaches and indicate areas of high potential for short- and longer term efficacy." @default.
- W3216383239 created "2021-12-06" @default.
- W3216383239 creator A5014350987 @default.
- W3216383239 creator A5075632907 @default.
- W3216383239 creator A5083767342 @default.
- W3216383239 date "2022-01-01" @default.
- W3216383239 modified "2023-10-14" @default.
- W3216383239 title "Translation of New and Emerging Therapies for Genetic Cardiomyopathies" @default.
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