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- W4205128823 startingPage "333" @default.
- W4205128823 abstract "Medulloblastoma is a rare malignancy of the posterior cranial fossa. Although until now considered a single disease, according to the current WHO classification, it is a heterogeneous tumor that comprises multiple molecularly defined subgroups, with distinct gene expression profiles, pathogenetic driver alterations, clinical behaviors and age at onset. Adult medulloblastoma, in particular, is considered a rarer orphan entity in neuro-oncology practice because while treatments have progressively evolved for the pediatric population, no practice-changing prospective, randomized clinical trials have been performed in adults. In this scenario, the toughest challenge is to transfer the advances in cancer genomics into new molecularly targeted therapeutics, to improve the prognosis of this neoplasm and the treatment-related toxicities. Herein, we focus on the recent advances in targeted therapy of medulloblastoma based on the new and deeper knowledge of disease biology." @default.
- W4205128823 created "2022-01-25" @default.
- W4205128823 creator A5019091770 @default.
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- W4205128823 creator A5063327760 @default.
- W4205128823 creator A5069993810 @default.
- W4205128823 creator A5087336206 @default.
- W4205128823 date "2022-01-11" @default.
- W4205128823 modified "2023-09-25" @default.
- W4205128823 title "Molecular Targeted Therapies: Time for a Paradigm Shift in Medulloblastoma Treatment?" @default.
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